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Gene therapy restores hearing in deaf mice

13-Jul-2015

Key points from article :

Targeted delivery of functioning TMC1 gene to hair cells in cochlea using engineered virus AAV1.

TMC1 accounts for 4 to 8 percent of genetic deafness. Clinical trials of gene therapy for humans expected within 5 to 10 years.

The study was published in the Science Translational Medicine journal.

Mentioned in this article:

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F.M. Kirby Neurobiology Center

Largest basic neuroscience research enterprise at a U.S. hospital.

Jeffrey Holt

Professor of Otolaryngology and Neurology at Harvard Medical School.

Science Translational Medicine

Journal that publish papers with topics related to translational medicine

Topics mentioned on this page:
Gene Therapy