Gene Therapy
Restoring the body with gene therapy.
Resources
Tap on icon for description, click on resource name for more details.
Company that develops and commercializes synthetic promoters to control gene expressions and regulations
Company that invests in scientific innovation to create transformative medicines for people with serious and life-threatening diseases
Store providing chemicals, equipment and materials on a scale and price that a DIY Scientist can use and afford.
Company dedicated to advancing genetic therapies in order to treat patients living with serious genetic diseases.
Gene Therapy Blog Posts
Perfect storm for gene therapy?
30-Jan-2014
Six of the best from Ray's newsletter
18-Jun-2013
Repairing damaged hearts - first step to rejuvenation
02-Jun-2013
Recent News
New CRISPR gene-editing drug for a rare protein-misfolding disorder
pharmaphorum - 28-Jun-2021
Phase 1 trial reports, single dose of the drug cuts protein levels by 87% in ATTR amyloidosis
Read more...Brain can learn to see again using algae proteins
BBC - 24-May-2021
Optogenetics bring back vision partially with light sensing proteins - new hope for the blind
Read more...New gene therapy technique, CopyCatcher, more accurate in fruit flies
SciTechDaily - 11-May-2021
Targets precise location of mutated gene rather than tagging on anywhere
Read more...Gene therapy preserved memory and learning in mice with Alzheimer's
Lifespan.io (LEAF) - 11-May-2021
Boosting a vital protein, Caveolin-1, this new technique offers hope against neurodegenerative diseases
Read more...Inherited blindness can now be cured with gene therapy
BBC - 29-Apr-2021
A breakthrough gene therapy restores eyesight in patients with rare eye disease
Read more...
