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Gene Therapy News

The young founder teaching big pharma a new way to reverse aging

The young founder teaching big pharma a new way to reverse aging

LEVITY - 21-Nov-2025

Targeted epigenetic editing could deliver durable, precise therapies for aging-related diseases

Gene-editing therapy shows powerful one-dose reduction in harmful cholesterol

Gene-editing therapy shows powerful one-dose reduction in harmful cholesterol

Independent - 10-Nov-2025

CRISPR therapy cut LDL and triglycerides by roughly 50% after a single infusion

Regeneron’s gene therapy helps kids hear naturally again

Regeneron’s gene therapy helps kids hear naturally again

FierceBiotech - 12-Oct-2025

Early results show hope for future hearing loss treatments

Gene therapy shows breakthrough success in Huntington’s disease trial

Gene therapy shows breakthrough success in Huntington’s disease trial

BBC - 25-Sep-2025

New treatment slows Huntington’s by 75%, offering patients hope of longer, better lives

MIT scientists engineer ultra-precise prime editors for safer gene editing

MIT scientists engineer ultra-precise prime editors for safer gene editing

The Scientist - 18-Sep-2025

New “vPE” tool cuts DNA errors 465-fold, boosting accuracy for future cell therapies

Safer DNA and RNA delivery tested in mice and monkeys

Safer DNA and RNA delivery tested in mice and monkeys

Live Forever Club - 17-Sep-2025

This could help treat many diseases by fixing problems at the source

Gene therapy is emerging as a powerful tool to target ageing at the genetic level

Gene therapy is emerging as a powerful tool to target ageing at the genetic level

Live Forever Club - 04-Aug-2025

Special techniques can improve body repair, energy, and reduce age-related illness

The future of weight loss might be one injection away

The future of weight loss might be one injection away

Live Forever Club - 18-Jul-2025

This may be a way to treat lifestyle diseases at the root, biologically and sustainably

Mitochondrial gene editing breakthrough in human cells

Mitochondrial gene editing breakthrough in human cells

Genetic Engineering & Biotechnology News (GEN) - 24-Jun-2025

Scientists restore mitochondrial function using precise, CRISPR-free gene editing tools

Splicebio raises $135m to advance gene therapy for eye disease

Splicebio raises $135m to advance gene therapy for eye disease

FierceBiotech - 11-Jun-2025

SB-007 enters phase 1/2 trials to restore vision in Stargardt disease using novel splicing tech

Stanford scientists unveil CRISPR tool to regrow damaged nerve cells

Stanford scientists unveil CRISPR tool to regrow damaged nerve cells

Stanford University - 21-May-2025

New tool guides RNA to injury sites in neurons, offering hope for neurodegenerative therapies

Wireless gene control: nanoparticles enable remote programming of therapeutic proteins

Wireless gene control: nanoparticles enable remote programming of therapeutic proteins

Phys.org - 18-May-2025

Magnetic fields trigger gene expression in cells via ROS-sensitive nanoparticle interfaces

Fractyl unveils gene therapy that mimics natural GLP-1 for diabetes and obesity

Fractyl unveils gene therapy that mimics natural GLP-1 for diabetes and obesity

Fractyl - 17-May-2025

Therapy cut blood sugar by >200 mg/dL & doubled insulin with 5x less GLP-1 than standard drugs

New gene tool could treat diseases by adding whole working genes

New gene tool could treat diseases by adding whole working genes

Live Science - 16-May-2025

More testing and funding are needed before it can be used in people

Breaking barriers: A new nanoparticle delivers drugs directly inside cells

Breaking barriers: A new nanoparticle delivers drugs directly inside cells

Wyss Institute - 15-May-2025

ENTER system bypasses cell traps to deliver gene therapies precisely and safely

One shot to the heart: gene editing breakthrough lowers cholesterol for life

One shot to the heart: gene editing breakthrough lowers cholesterol for life

Inside Precision Medicine - 15-Apr-2025

Verve’s one-time gene therapy could end daily cholesterol meds

Extinct no more: dire wolves reborn through breakthrough science

Extinct no more: dire wolves reborn through breakthrough science

Independent - 08-Apr-2025

Ancient DNA and gene editing revive the Ice Age predator after 10,000 years

China’s RiboX beats rivals to launch first circular RNA clinical trial

China’s RiboX beats rivals to launch first circular RNA clinical trial

Endpoints News - 04-Apr-2025

A stealthy Shanghai startup pioneers a longer-lasting, safer alternative to mRNA and gene therapies

Tenaya raises $52.5m to push forward gene therapy trials

Tenaya raises $52.5m to push forward gene therapy trials

Longevity Technology - 05-Mar-2025

The biotech firm accelerates clinical trials for TN-201 and TN-401, targeting genetic heart disease

From woolly mice to mammoth-like elephants: A bold experiment in genetic engineering

From woolly mice to mammoth-like elephants: A bold experiment in genetic engineering

BBC - 04-Mar-2025

Scientists aim to create cold-adapted elephants to restore Arctic ecosystems

Vertex ends gene editing deal with Verve amid R&D shift

Vertex ends gene editing deal with Verve amid R&D shift

FierceBiotech - 27-Feb-2025

Verve regains full rights to its liver disease program as it moves forward independently

Gene therapy restores hearing in children with rare deafness

Gene therapy restores hearing in children with rare deafness

FierceBiotech - 24-Feb-2025

Regeneron’s DB-OTO offers new hope for genetic hearing loss

Gene therapy restores sight in children born blind

Gene therapy restores sight in children born blind

BBC - 21-Feb-2025

A groundbreaking trial shows how early genetic treatment can transform vision and improve lives

Bio-ReCell and BIOTEM collaborate to enhance T-cell therapy

Bio-ReCell and BIOTEM collaborate to enhance T-cell therapy

Bio-ReCell - 19-Feb-2025

The partnership adds BIOTEM’s antibodies to Bio-ReCell’s kits to boost cell therapy precision and scale

NHS launches groundbreaking sickle cell gene therapy

NHS launches groundbreaking sickle cell gene therapy

BBC - 31-Jan-2025

Transforming lives with a groundbreaking cure for sickle cell disease


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