Gene Therapy News

Scientists overcome hurdles to design human artificial chromosomes

Singularity Hub - 26-Mar-2024

New technique delivers more genetic material, paving way for safer & effective gene therapies

Nanoscope's gene therapy offers hope for patients blinded by inherited retinal disease

FierceBiotech - 26-Mar-2024

Phase 2 trial results show significant vision improvement, plans for FDA approval

Gene therapy for rare brain disease sets a new pricing record at $4.25 million

FiercePharma - 20-Mar-2024

Its record-breaking price raises questions about affordability and access

Novel approach effectively silences cholesterol genes in mice for a year

News Medical - 01-Mar-2024

This could lead to long-lasting cholesterol treatments without genetic damages

Invisible stem cells treat disease without triggering immune response

Nature - 28-Feb-2024

Genetically-modified stem cells avoid immune rejection, paving way for universal therapies for everyone

Diabetic monkeys regain insulin independence after transplant of unique insulin cells

Live Forever Club - 23-Feb-2024

This could lead to a safer and better treatment for type 1 diabetes.

RNA editing therapies for genetic diseases signify medical research progress

Nature - 16-Feb-2024

Unlike editing DNA itself, this new approach makes temporary changes to RNA

Rejuvenate Bio partners with animal company to develop gene therapy for canine osteoarthritis

Biospace - 14-Feb-2024

Single dose injection targets root causes, offering long-term relief & improved quality of life

Fractyl raised $110 million to develop treatments for obesity and diabetes

Longevity Technology - 05-Feb-2024

They picked RJVA-001, a gene therapy, as their first clinical candidate

Dresden merges recombinases & DNA-binding domains for tailored gene editing

Medical Xpress - 31-Jan-2024

The research offers safer and more precise ways to treat genetic disorders

A CRISPR gene editing technique has cured hereditary angioedema in a single-dose

New Scientist - 31-Jan-2024

It demonstrated a remarkable cure rate, rather than merely offering a treatment

MeiraGTx at the forefront of gene therapy for cancer, obesity, and vision loss

Evening Standard - 21-Dec-2023

London biotech promises revolutionary therapies by replacing faulty genes & flipping gene switches

ARCUS gene editing technology effectively eliminates mutant mitochondrial DNA

Biospace - 04-Dec-2023

Potential therapeutic approach for mitochondrial and other genetic diseases

UK's approval of casgevy paves the way for gene-edited treatment of blood disorders

BBC - 16-Nov-2023

Casgevy offers hope for patients with sickle cell disease and beta thalassemia

Single-dose gene-editing therapy offers permanent solution to high cholesterol levels

New Scientist - 14-Nov-2023

Early results show promise in eliminating the need for lifelong statins

A new gene therapy treatment has helped deaf children hear for the first time

MIT Technology Review - 27-Oct-2023

Treatment delivers a working copy of a missing gene to the inner ear

Beyond CRISPR: Fanzors, a new era of programmable DNA editing tools

Massachusetts Institute of Technology (MIT) - 13-Oct-2023

Scientists discover a vast array of RNA-guided enzymes in diverse organisms

Broken string secures $15m to make cell and gene therapy safer, more accessible

Longevity Technology - 19-Sep-2023

Company's INDUCE-seq platform could revolutionise cell & gene therapy efficiency

Amber Bio secures $26M funding to advance new gene editing technologies

Longevity Technology - 07-Aug-2023

By editing RNA instead of DNA, the company aims to treat multiple undruggable genetic diseases safely

Voyager's new gene therapy targets amyloid plaques in Alzheimer's disease

FierceBiotech - 04-Aug-2023

New treatment approach could be more effective in lowering the risk of serious side effects

Novel method facilitates single-cell expansion of gene edited stem cells

Lifespan.io (LEAF) - 17-Jul-2023

Its polymer-supplemented culture system enables cell expansion without harmful mutations

Gene therapy restores partial red colour vision in total colour blindness patients

New Scientist - 10-Jul-2023

Despite the limited improvement, gene therapy offers hope for future breakthroughs in restoring vision

Game-changing bacteriophage could revolutionize gene therapy

New Scientist - 30-May-2023

Ability to carry vast amounts of DNA and other molecules promises substantial advancements in gene and cell therapies

Therapeutic applications of base editing clears girl's leukemia

BBC - 11-Dec-2022

Base editing can soon be a part in taking control of our genomes to fight genetic diseases

CRISPR based PASTE (Programmable Addition via Site-specific Targeting Elements) tool designed

MIT Media Lab - 24-Nov-2022

The new PASTE tool replaces faulty genes in a safer and more efficient way