Gene therapy shows breakthrough success in Huntington’s disease trial
BBC - 25-Sep-2025New treatment slows Huntington’s by 75%, offering patients hope of longer, better lives
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New treatment slows Huntington’s by 75%, offering patients hope of longer, better lives
This could help treat many diseases by fixing problems at the source
Special techniques can improve body repair, energy, and reduce age-related illness
This may be a way to treat lifestyle diseases at the root, biologically and sustainably
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More testing and funding are needed before it can be used in people
ENTER system bypasses cell traps to deliver gene therapies precisely and safely
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Scientists aim to create cold-adapted elephants to restore Arctic ecosystems
Verve regains full rights to its liver disease program as it moves forward independently
Regeneron’s DB-OTO offers new hope for genetic hearing loss
A groundbreaking trial shows how early genetic treatment can transform vision and improve lives
The partnership adds BIOTEM’s antibodies to Bio-ReCell’s kits to boost cell therapy precision and scale
Transforming lives with a groundbreaking cure for sickle cell disease
A partnership advancing synthetic AAV vectors to tackle gene therapy challenges
Basecamp expands AI and genetic tools to create fast, programmable gene therapies
Revolutionary gene therapy disables cancer cells’ mitochondria, sparing healthy tissue
This treatment helped restore heart function to near-normal levels
BioViva focuses on translating this research into therapies