Precision genetics: unlocking the secrets of mutation
Harvard University - 13-Nov-2024A revolutionary tool targets specific genes, advancing our understanding of evolution and disease
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A revolutionary tool targets specific genes, advancing our understanding of evolution and disease
They aim to use AI-driven capsid design for delivery for complex treatments
Tests in mice and human cells show long-lasting gene correction
A new breakthrough in nanotechnology offers a non-invasive way to access the cell's genetic material
A promising one-time treatment approach for arrhythmogenic cardiomyopathy
This revolutionary treatment could eliminate the need for lifelong blood transfusions
Company is particularly focusing on less invasive treatments for dry AMD and XLRP
The therapy is initially available at eight centers across the UK
Potential for advancements in medicine, agriculture, and other fields
Boosting IRAK-M protein protects retina in the eyes and paves way for potential AMD treatment
Company aims to improve protein production in genetic medicine
Therapy offers hope for a potential cure for certain types of hearing loss
Treatment shows improved blood flow, exercise tolerance and reduced symptoms
AI-powered platform predicts drugs for age-related diseases with 80% accuracy
This could lead to safer and more effective treatments for genetic diseases
New technique delivers more genetic material, paving way for safer & effective gene therapies
Phase 2 trial results show significant vision improvement, plans for FDA approval
This experimental therapy targets a common metabolic issue in Retinitis Pigmentosa
Its record-breaking price raises questions about affordability and access
This could lead to long-lasting cholesterol treatments without genetic damages
Genetically-modified stem cells avoid immune rejection, paving way for universal therapies for everyone
This could lead to a safer and better treatment for type 1 diabetes.
Unlike editing DNA itself, this new approach makes temporary changes to RNA
Single dose injection targets root causes, offering long-term relief & improved quality of life
They picked RJVA-001, a gene therapy, as their first clinical candidate