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Gene Therapy News

Precision genetics: unlocking the secrets of mutation

Precision genetics: unlocking the secrets of mutation

Harvard University - 13-Nov-2024

A revolutionary tool targets specific genes, advancing our understanding of evolution and disease

Dyno partners with Roche to enhance gene therapy for brain diseases

Dyno partners with Roche to enhance gene therapy for brain diseases

Longevity Technology - 25-Oct-2024

They aim to use AI-driven capsid design for delivery for complex treatments

Nanoparticles deliver tools to fix gene mistakes in lung cells

Nanoparticles deliver tools to fix gene mistakes in lung cells

The Scientist - 15-Oct-2024

Tests in mice and human cells show long-lasting gene correction

Nanopillars unlock the nucleus without harming cells

Nanopillars unlock the nucleus without harming cells

Science Daily - 02-Oct-2024

A new breakthrough in nanotechnology offers a non-invasive way to access the cell's genetic material

Rejuvenate Bio secures $4M to advance gene therapy for a devastating heart disease

Rejuvenate Bio secures $4M to advance gene therapy for a devastating heart disease

BioProcess International - 27-Aug-2024

A promising one-time treatment approach for arrhythmogenic cardiomyopathy

Gene-editing offers NHS patients potential cure for beta thalassemia

Gene-editing offers NHS patients potential cure for beta thalassemia

BBC - 08-Aug-2024

This revolutionary treatment could eliminate the need for lifelong blood transfusions

Beacon Therapeutics secures $170M to develop gene therapies for retinal diseases

Beacon Therapeutics secures $170M to develop gene therapies for retinal diseases

Longevity Technology - 05-Jul-2024

Company is particularly focusing on less invasive treatments for dry AMD and XLRP

NHS offers novel gene therapy for haemophilia B, potentially curing patients

NHS offers novel gene therapy for haemophilia B, potentially curing patients

BBC - 27-Jun-2024

The therapy is initially available at eight centers across the UK

New gene-editing tool, 'bridge editing,' surpasses CRISPR in precise DNA alterations

New gene-editing tool, 'bridge editing,' surpasses CRISPR in precise DNA alterations

New Scientist - 26-Jun-2024

Potential for advancements in medicine, agriculture, and other fields

Scientists discover key protein that could prevent age-related vision loss

Scientists discover key protein that could prevent age-related vision loss

Independent - 05-Jun-2024

Boosting IRAK-M protein protects retina in the eyes and paves way for potential AMD treatment

ExpressionEdits secures $13M for developing AI-powered gene therapy

ExpressionEdits secures $13M for developing AI-powered gene therapy

Longevity Technology - 03-Jun-2024

Company aims to improve protein production in genetic medicine

Toddler born with hearing loss can now hear thanks to new gene therapy trial

Toddler born with hearing loss can now hear thanks to new gene therapy trial

The Guardian - 09-May-2024

Therapy offers hope for a potential cure for certain types of hearing loss

Gene therapy triggers natural blood vessel growth in angina patients

Gene therapy triggers natural blood vessel growth in angina patients

EurekAlert! - 02-May-2024

Treatment shows improved blood flow, exercise tolerance and reduced symptoms

Gordian Biotechnology raises $60M to accelerate gene therapy discovery

Gordian Biotechnology raises $60M to accelerate gene therapy discovery

Longevity Technology - 26-Apr-2024

AI-powered platform predicts drugs for age-related diseases with 80% accuracy

AI designs a more precise CRISPR gene editor for use in human cells

AI designs a more precise CRISPR gene editor for use in human cells

Singularity Hub - 25-Apr-2024

This could lead to safer and more effective treatments for genetic diseases

Scientists overcome hurdles to design human artificial chromosomes

Scientists overcome hurdles to design human artificial chromosomes

Singularity Hub - 26-Mar-2024

New technique delivers more genetic material, paving way for safer & effective gene therapies

Nanoscope's gene therapy offers hope for patients blinded by inherited retinal disease

Nanoscope's gene therapy offers hope for patients blinded by inherited retinal disease

FierceBiotech - 26-Mar-2024

Phase 2 trial results show significant vision improvement, plans for FDA approval

Columbia scientists use CRISPR gene editing to boost energy production in eye cells

Columbia scientists use CRISPR gene editing to boost energy production in eye cells

Medical Xpress - 21-Mar-2024

This experimental therapy targets a common metabolic issue in Retinitis Pigmentosa

Gene therapy for rare brain disease sets a new pricing record at $4.25 million

Gene therapy for rare brain disease sets a new pricing record at $4.25 million

FiercePharma - 20-Mar-2024

Its record-breaking price raises questions about affordability and access

Novel approach effectively silences cholesterol genes in mice for a year

Novel approach effectively silences cholesterol genes in mice for a year

News Medical - 01-Mar-2024

This could lead to long-lasting cholesterol treatments without genetic damages

Invisible stem cells treat disease without triggering immune response

Invisible stem cells treat disease without triggering immune response

Nature - 28-Feb-2024

Genetically-modified stem cells avoid immune rejection, paving way for universal therapies for everyone

Diabetic monkeys regain insulin independence after transplant of unique insulin cells

Diabetic monkeys regain insulin independence after transplant of unique insulin cells

Live Forever Club - 23-Feb-2024

This could lead to a safer and better treatment for type 1 diabetes.

RNA editing therapies for genetic diseases signify medical research progress

RNA editing therapies for genetic diseases signify medical research progress

Nature - 16-Feb-2024

Unlike editing DNA itself, this new approach makes temporary changes to RNA

Rejuvenate Bio partners with animal company to develop gene therapy for canine osteoarthritis

Rejuvenate Bio partners with animal company to develop gene therapy for canine osteoarthritis

Biospace - 14-Feb-2024

Single dose injection targets root causes, offering long-term relief & improved quality of life

Fractyl raised $110 million to develop treatments for obesity and diabetes

Fractyl raised $110 million to develop treatments for obesity and diabetes

Longevity Technology - 05-Feb-2024

They picked RJVA-001, a gene therapy, as their first clinical candidate


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