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Drug approved as alternative method to CRISPR

Patisiran is a new drug capable of silencing genes based on RNA interference technology

21-Aug-2018

Key points from article :

FDA approve new family of drugs able to cure inherited diseases.

Alnylam has created patisiran to treat genetic nerve damage.

Based on RNA interference (RNAi) which can silence genes.

RNAi can potentially cure any disease caused by “bad” proteins.

These diseases include stroke, Alzheimer’s, and high cholesterol.

Targets root cause of condition rather than just its symptoms.

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Food and Drug Administration (FDA)

Ensuring safety of drugs, medical supplies and food which is used daily.

Scott Gottlieb

American physician and investor.

Topics mentioned on this page:
Gene Therapy