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CRISPR Gene Editing Cures Mice of Sickle Cell Disease

12-Oct-2016

Key points from article :

CRISPR used to correct mutated hematopoietic stem cells.

Corrected blood stem cells produced healthy hemoglobin.

Engineered stem cells remained in circulation for at least four months.

Safety analyses needed before human trials.

The study was published in the Science Translational Medicine journal.

Mentioned in this article:

Click on resource name for more details.

Children's Hospital Oakland Research Institute (CHORI)

Biomedical research institute affiliated with California's pediatric medical center.

Jacob Corn

Professor of Genome Biology at ETH Zurich.

Science Translational Medicine

Journal that publish papers with topics related to translational medicine

University of California, Berkeley

Public land-grant research university

University of Utah School of Medicine

School of medicine at the University of Utah.

Topics mentioned on this page:
Gene Therapy