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Trial shows Huntington's drug could slow progress of disease

11-Dec-2017

Key points from article :

Drug suppresses the effects of the Huntington’s mutation that causes irreversible damage to the brain.

Huntington’s is caused by a single gene defect that is passed down through families.

Ionis-HTTRx works by intercepting the messenger molecule before the harmful protein can be made.

University College London led the phase 1 trial of synthetic strand of DNA drug.

Could potentially be adapted to target Alzheimer’s and Parkinson’s.

Mentioned in this article:

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Ionis Pharmaceuticals

Leader in discovering and developing RNA-targeted therapeutics.

Sarah Tabrizi

Professor of Clinical Neurology at UCL Institute of Neurology.

University College London (UCL)

Diverse global community of world-class academics, students, industry links, external partners, and alumni

Topics mentioned on this page:
Mental Health