Join the club for FREE to access the whole archive and other member benefits.

RNA editing therapies for genetic diseases signify medical research progress

Unlike editing DNA itself, this new approach makes temporary changes to RNA

16-Feb-2024

Key points from article :

Scientists are developing new therapies that focus on editing RNA instead of DNA (like CRISPR).

RNA editing involves changing messenger RNA (mRNA), which carries instructions for making proteins, potentially fixing problems caused by genetic diseases.

Two RNA-editing therapies have recently been approved for clinical trials, making them the first of their kind to reach this stage of testing.

Researchers believe RNA editing could be safer and more versatile than DNA editing techniques, but it also comes with technical challenges.

The approval of clinical trials shows that RNA editing is a promising area of research with the potential to revolutionize how we treat genetic diseases.

This article was published in the journal Nature.

Mentioned in this article:

Click on resource name for more details.

Nature

Scientific journal covering research from a variety of academic disciplines, mostly in science and technology

Topics mentioned on this page:
Gene Therapy
RNA editing therapies for genetic diseases signify medical research progress