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Fixing the genes to cure inherited blindness

Crispr gene editing is a great but a dangerous tool

04-Mar-2020

Key points from article :

Scientists have used Crispr-Cas9 inside a person’s body for the first time.

Operated on DNA using this gene-editing tool to treat an inherited form of blindness.

Edited the mutation by making two cuts on either side of it and allowing the ends to reconnect.

The editing of gene should hold for the lifetime since cells in the retina do not divide.

Have to wait for a month to see if the procedure yields expected results.

If successful people suffering from Leber congenital amaurosis would be able to see the world again.

Mentioned in this article:

Click on resource name for more details.

Allergan

Pharmaceutical company that acquires, develops, and markets brand name drugs.

Casey Eye Institute

Medical center specialising in opthalmology

Charles Albright

Chief Scientific Officer at Editas Medicine

Editas Medicine

Genome editing company.

Eric Pierce

Professor of Ophthalmology

Jason I. Comander

Assistant Professor of Ophthalmology at Harvard Medical School

Jean Bennett

Professor of Ophthalmology

Kiran Musunuru

Cardiologist, geneticist, and gene editor

Topics mentioned on this page:
Gene Therapy, Vision (health)