Molecular Therapy is an open-access journal, dedicated to promoting the sciences in genetics, medicine, and biotechnology. It is a leading journal in the areas of gene transfer, vector development and design, stem cell manipulation, development of gene-, peptide-, protein-, oligonucleotide-, and cell-based therapeutics to correct genetic and acquired diseases, vaccine development, pre-clinical target validation, safety/efficacy studies, and clinical trials.

2019 impact factor is 8.986.