A CRISPR gene editing technique has cured hereditary angioedema in a single-dose
New Scientist - 31-Jan-2024It demonstrated a remarkable cure rate, rather than merely offering a treatment
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CRISPR/Cas9 based genome editing company
Intellia Therapeutics is a leading clinical-stage company developing potentially curative gene editing treatments for people living with severe and life-threatening diseases. Uses CRISPR/Cas9 system to harness genome-editing technology for human therapeutic use. It has partnerships with Novartis and Regeneron.
Intellia is committed to making CRISPR/Cas9-based medicines a reality for patients suffering from genetic diseases and to creating novel engineered cell therapies for various cancers and autoimmune diseases.
Visit website: https://www.intelliatx.com/
Details last updated 03-Jul-2021
It demonstrated a remarkable cure rate, rather than merely offering a treatment
Phase 1 trial reports, single dose of the drug cuts protein levels by 87% in ATTR amyloidosis