Human trials using CRISPR to cure genetically inherited blindness
Heritable disease Leber congenital amaurosis(LCA) causes complete loss of vision.
Will provide a health version of a gene that patients lack through a subretinal injection.
This will be done using the CRISPR gene editing technology.
But this injected gene will not pass into future generations.
Up to 18 people from age 3 onwards will take part in this clinical trial in US.
These trials will be conducted by the pharmaceutical companies Editas Medicine and Allergan.
Mentioned in this article:
Allergan - Pharmaceutical company that acquires, develops, and markets brand name drugs.
Editas Medicine - Genome editing company.